Inside every cell, thousands of molecular signals collide, overlap, and compensate, obscuring the true drivers of gene ...

The Food and Drug Administration aims to evaluate treatments for rare diseases based on plausible evidence that they would work — without requiring a clinical trial first.

FDA Commissioner Marty Makary says the agency wants to remove barriers for patients suffering from rare genetic conditions.

Engineers at the University of Pennsylvania and Rice University have refined a technology for editing individual genetic "base pairs" to a new level of precision, opening the door to safer, more ...

Engineers at the University of Pennsylvania and Rice University have refined a technology for editing individual genetic ...

Researchers have found that a new base-editing gene therapy can help treat a rare neurodevelopmental disorder called Snijders Blok–Campeau syndrome caused by mutations in the CHD3 gene. A specialized ...

A version of this Priestley Medal address will be presented at the American Chemical Society Spring 2026 meeting ...

Researchers from New England Biolabs and Yale University have created a system for engineering the first fully synthetic ...

For nearly four billion years, life on Earth evolved blindly. Natural selection tinkered, mutations accumulated, and ...

Raised in Surprise, a northwest suburb of Phoenix, Valencia’s first job was at the Cholla branch of the Phoenix Public ...

But they disagree on whether studying social genomics—elucidating any potential genetic contributions to behaviors ranging from mental illnesses to educational attainment to political affiliation—can ...