Genethon, a pioneering gene therapy research organization created by the AFM-Telethon, marks Rare Disease Day February 28, ...

During his visit to the Kingdom of Bahrain, the Director-General of the World Health Organization (WHO), Dr. Tedros Adhanom ...

Q4 2024 Earnings Conference Call February 26, 2025 4:30 PM ET. Company Participants. Katie Hogan - Senior Director-Corporate Communications and Investo ...

In the phase 1/2 INSPIRE DUCHENNE trial, interim data showed an average microdystrophin expression of 110% among participants ...

Looking forward, greater use of column chromatography technologies in vector manufacturing could facilitate the adoption of ...

CRISPR is like an editor that can rewrite DNA letter by letter or gene by gene, to remove harmful mutations or add protective ...

A single injection of a healthy gene allowed blind children to recognize objects, shapes, and even read — offering hope for ...

PRGN-2012—which Precigen has begun to call by its generic name of zopapogene imadenovec—is a gene therapy designed to elicit immune responses directed against cells infected with human papillomavirus ...

Retinal gene therapy advancements may rewrite the book on treatments for age-related macular degeneration and diabetic eye diseases.

Reducing the number of intravitreal injections to treat age-related macular degeneration (AMD) is a top priority in current ...

As FDA seeks to rehire some fired employees, Donald Trump threatens to enact tariffs on pharma companies unless they reshore manufacturing; another lawsuit hits the complex GLP-1 compounding space as ...

Early results from the company’s single-arm trial saw the therapy able to partially repair the chemical responsible for ...