Durham-based Precision BioSciences, a gene-editing company, has received regulatory clearance to begin a clinical study of its potential treatment for Duchenne muscular dystrophy (DMD), a rare ...
Allergy research has historically relied on traditional systems such as 2D cell cultures and mouse models to uncover mechanisms underlying allergic ...
Rare Disease Day is held on the last day of February to raise awareness for rare diseases and address drug development ...
The US leads the world in ag biotech, but that lead is eroding, not in the lab, but in the gap between discovery and ...
Chiquita Brands International is betting that the next chapter in bananas won’t be entirely written in a lab with gene ...
New FDA guidelines for personalized genomic drug development are a step forward in advancing new therapies for ultrarare diseases, but industry leaders need further clarification.
Recent medical advances in gene and cell therapies have renewed hope for some patients with aggressive blood cancers.
Researchers at the Sanford Stem Cell Institute have taken the fight against rare diseases to the lab, to patients’ bedsides ...
A new CRISPR-based tool that is directly used on patients' cancer cells can identify genes and regulatory elements driving ...
Gene therapy and gene editing are marvels of modern biotechnology, providing revolutionary techniques for fixing genetic abnormalities. Gene therapy introduces functional genetic material to ...
Scientists at Texas A&M are turning an everyday pick-me-up into a high-tech medical switch. By combining caffeine with CRISPR ...