The American Journal of Managed Care

Progress in Precise Gene Expression Control With CRISPR-Cas12f

An innovative CRISPR-Cas12f-based activator system may hold significant potential in the future of gene therapy and biological research, suggest researchers of a new study. The study highlights the ...
BioSpace

Strand Therapeutics Doses First Patients with STX-003, a Systemic Programmable mRNA Therapy Designed for Tumor-Selective Activation

First-in-human study evaluates Strand’s ability to unlock the potential of systemic mRNA-encoded medicines with an IL-12 ...
BIOENGINEER

Chronic Lung Infection Surprisingly Sustains Gene Therapy Expression in Cystic Fibrosis Rat Lungs

New research in cystic fibrosis rats shows that chronic Pseudomonas aeruginosa lung infection does not hinder lentiviral vector gene transfer and may actually prolong transgene expression compared ...
GEN

Genetic “Dimmer Switch” Offers Precise Gene Expression Control

Scientists at the MRC Laboratory of Medical Sciences (LMS) have discovered a DNA-based “dimmer switch” that regulates the activity of a critical developmental gene, Cdx2. This work could pave the way ...
Yahoo Finance

Expression Therapeutics Receives FDA Fast Track and Rare Pediatric Disease Designations for Investigational Stem Cell Therapy for Hemophilia A

ATLANTA, April 29, 2026 /PRNewswire/ -- Expression Therapeutics, Inc., a clinical-stage biopharmaceutical company developing a curative autologous stem cell therapy for hemophilia A, today announced ...
streetinsider

Expression Therapeutics Receives FDA Fast Track and Rare Pediatric Disease Designations for Investigational Stem Cell Therapy for Hemophilia A

Dual Designations Affirm Significant Unmet Need; Multi-Year Phase 1 Data Published in the New England Journal of Medicine Underpin Advancement to Phase 2 ATLANTA, April 29, 2026 /PRNewswire/ -- ...